Topic

NORD and the Rare Disease Diversity Coalition form a partnership to shed light on access for underrepresented patients.

For people who live with rare and chronic illness, the holiday whirlwind sometimes calls for “plan B.”

Arthur is stepping forward for those also living with chronic inflammatory demyelinating polyneuropathy (CIDP).

CSL’s Ellyn Getz, Director of R&D Patient Partnerships, visits the Advarra podcast to talk about how clinical research studie…

The bleeding disorder hemophilia B goes by an alternate name all because of a 5-year-old boy.

It’s time for holiday shopping! We recommend books, jewelry and other stocking stuffers to help spread the word about rare di…

KING OF PRUSSIA, PA, USA This historic approval provides a new treatment option that reduces the rate of annual bleeds, re…

5 ways to stay healthy as the winter holidays approach, bringing family togetherness, office parties and some familiar uncert…

A very smart part of the immune system, T cells remember infections that your body has experienced before, an immunologist sa…

For 20 years, the program has offered sports training, educational sessions and a weekend of community for kids and teens who…

Patients who have respiratory conditions often require supplemental oxygen, but getting what they need to live full lives can…

A CSL R&D leader explains how we’re accelerating global research impact through a strategic gene therapy alliance with scient…